A person with Duchenne muscular dystrophy has become the first to receive a novel gene-editing therapy in a new U.S. clinical ...

Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...

Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The disease is chronic and begins in childhood. The life expectancy of affected ...

Coordination of Care for Patients with Duchenne Muscular Dystrophy: Teamwork is Everything Duchenne Muscular Dystrophy: Speaking with Patients and Families About Advanced Care ...

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine Today, the world stands at a crossroads in genetic medicine ...

Sarepta Therapeutics demanded a prominent patient advocacy organization censor a video that contained pointed criticism of the company’s recently approved gene therapy for Duchenne muscular dystrophy, ...

CureDuchenne Ventures aims to raise a $50 million fund to back startups seeking to cure the genetic disease Duchenne muscular ...

While skeletal muscle is abundant in the human body, it been difficult for researchers to derive muscle cells from precursor cells or culture in sufficient quantities to study them. New research, ...

More than 30 rare muscular dystrophy types cause progressive muscle weakness from inherited gene mutations. Combined, they affect about 1 in 5,000 to 8,000 people. Common subtypes vary by age of onset ...

A cell therapy made from donor heart cells slowed the decline of cardiac function in boys and young men with Duchenne muscular dystrophy by roughly 91 percent over a year, according to results from a ...

This recognition highlights CHOP's long-standing commitment to providing world-class care and advancing clinical research for individuals living with Duchenne and Becker muscular dystrophy. The ...

TAS-205 showed no significant impact on motor function in patients with Duchenne muscular dystrophy (DMD), highlighting the ongoing search for effective treatments for the rare condition. Families ...