News

Muscular Dystrophy News7h

Duchenne MD gene-editing therapy nets orphan drug designation

A mouse model study of Precision BioSciences’ gene-editing therapy PBGENE-DMD found it produced long-term functional ...
Muscular Dystrophy News2d

Elevidys shipments for ambulatory DMD patients to resume

Sarepta will soon resume shipping Elevidys for ambulatory Duchenne muscular dystrophy patients after a review of safety data ...