The movement-related benefits of Itvisma were maintained or continued to deepen over about 15 months after treatment, trial ...

Columnist Sherry Toh usually cringes at people who stare, but a performative art project taught her something new about ...

Up to three years of Evrysdi treatment appears safe and may help presymptomatic children with SMA reach and maintain key milestones.

High doses of Spinraza may help stabilize or improve motor function for many people with SMA, per pooled clinical trial ...

Salanersen, a treatment candidate for spinal muscular atrophy (SMA) now in clinical testing, is safe and was shown to stabilize or improve motor function over at least one year of follow-up in ...

Columnist Ari Anderson recently enjoyed six weeks free from searching for new members of his nursing staff. Now, he's aiming ...

Mutations that cause spinal muscular atrophy (SMA) may lead to abnormalities in the development of cells in the spinal cord, a study found.

SMA newborn screening may help infants start treatment sooner, which researchers say could support better motor development outcomes.