Apitegromab improved motor function in SMA patients in a Phase 3 trial analysis, with stronger benefits seen in those treated earlier.

Biogen has launched a trio of Phase 3 trials to test salanersen, a new SMA treatment that aims to be a more convenient ...

Spinraza treatment led to sustained improvements in motor function in adults with SMA, according to a South Korean study.

For columnist Sherry Toh, the new TV series "The Beauty" dwells too much on the grief of living with a rare disease but ignores the strength.

Scholar Rock plans to resubmit its application seeking approval for apitegromab, an investigational muscle-strengthening therapy for SMA.

Today is Caregiver Appreciation Day and columnist Connie Chandler wants the caregivers in her life to know how much she appreciates them.

A new study found Spinraza treatment restores a key amino acid called taurine in SMA type 1, which may improve clinical ...

In honor of Rare Disease Day, columnist Halsey Blocher shines a light on the caregivers who make life possible for those with SMA.

The first patient has been dosed in a Phase 1/2 study of GB221, a next-generation gene therapy for SMA type 1.

Medical equipment and technology are crucial for columnist Ari Anderson, who lives with SMA, so malfunctions can quickly ...

Blood vessel damage in the spinal cord may play a role in nerve cell loss in spinal muscular atrophy, a new study suggests.

Columnist Helen Baldwin recalls the major life changes that preceded her introduction to the SMA community with the birth of ...