Treatment with Evrysdi (risdiplam) may modestly improve arm function for adults with spinal muscular atrophy (SMA), a new study indicates.

Columnist Connie Chandler is inspired by the Olympic athletes, who invite people all over the world to dream that anything is possible.

Children with SMA often struggle to get a good night's sleep, and their caregivers also report feeling sleep-deprived, a new ...

Early treatment helps with swallowing and eating for SMA kids, but new research is needed on the effects of disease-modifying ...

Guest writer Ronna Johnson feels privileged to support her son, Brandon, in living his best life, pursuing his goals, and ...

The blood creatinine-to-cystatin-c ratio may be a biomarker of Spinraza treatment response in children with SMA, a study in ...

Columnist Sherry Toh writes of her love for Disney's "Beauty and the Beast" and reimagines a production led by a person with a disability.

At first, columnist Connie Chandler wasn't sold on the idea of attending a global prom. But she was soon convinced it's a special night.

The strength of nerve electrical impulses in children with SMA can help predict their response to treatment with Spinraza, a study found.

Treatment with a high-dose regimen of Spinraza safely improved motor function in children with SMA, according to data from ...

Researchers described what they believe to be the first case of SMA type 4 presenting with a false enlargement of a muscle in the calf.

Women with SMA can experience successful pregnancies and positive birth outcomes. Pregnancy in SMA involves risks uch as breathing challenges and preterm birth. Multidisciplinary team care, including ...